cerebrotendinous xanthomatosis

ICD-10: E75.5MeSH: D019294ORPHA: 1651 Treatment Available

Overview

autosomal recessive form of xanthomatosis.

Available Treatments (1)

DrugFormStatusCountriesLead Time
chenodiol
Orphan
FDA Approved (2025)1

Classification & Codes

ICD-10 Code

E75.5

MeSH Code

D019294

Orphanet Code

ORPHA:165
cerebrotendinous xanthomatosis
ICD-10E75.5
MeSHD019294
OrphanetORPHA:165
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO