Chronic graft versus host disease

ORPHA: 999211 Treatment Available

Available Treatments (1)

DrugFormStatusCountriesLead Time
axatilimab
Orphan Cold Chain
Oral capsuleFDA Approved (2024)1

Clinical Presentation

Signs and symptoms associated with Chronic graft versus host disease, sourced from HPO and Orphanet clinical annotations.

Poor wound healingThickened skinIntermittent generalized erythematous papular rashXerostomiaRecurrent corneal erosionsPhotophobiaAbnormality of skin pigmentationKeratoconjunctivitis siccaAlopeciaOnycholysisBronchiectasisRecurrent infectionsElevated circulating hepatic transaminase concentrationNail dystrophyErythemaFood intoleranceAbnormal vagina morphologyHematuriaMuscle weaknessArthritisFlexion contractureAscitesPhimosisWeight lossPancytopeniaDiarrheaDysphagiaNauseaGastroesophageal refluxAbdominal painAbnormal esophagus morphologyAnorexiaEsophageal strictureDyspneaPneumothoraxPulmonary infiltratesPleural effusionArthralgiaMyalgiaEsophageal ulcerationAirway obstructionBronchiolitis obliteransEntrapment neuropathyMorpheaPainCoughAbnormal esophagus physiologyWheezingFasciitisUrinary bladder inflammationChest painSkin vesicleSkin ulcer

Classification & Codes

Orphanet Code

ORPHA:99921
Chronic graft versus host disease
OrphanetORPHA:99921
Treatments1 drug(s)
Symptoms on record53 signs
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO