Duchenne Muscular Dystrophy
ICD-10: G71.01MeSH: D020388ORPHA: 988962 Treatments Available
Overview
Duchenne muscular dystrophy (DMD) is a severe type of muscular dystrophy that primarily affects boys.
Available Treatments (2)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| vamorolone Orphan | Oral suspension | FDA Approved | 2 | — |
| delandistrogene moxeparvovec-rokl Orphan Cold Chain | Concentrate for solution for infusion | FDA Approved | 1 | — |
Clinical Presentation
Signs and symptoms associated with Duchenne Muscular Dystrophy, sourced from HPO and Orphanet clinical annotations.
Delayed speech and language developmentGlobal developmental delayMotor delaySpecific learning disabilityFlexion contractureCardiomyopathyRespiratory insufficiencyWaddling gaitScoliosisSkeletal muscle atrophyElevated circulating creatine kinase concentrationProgressive muscle weaknessProximal muscle weaknessCalf muscle hypertrophyCognitive impairment
Classification & Codes
ICD-10 Code
G71.01MeSH Code
D020388Orphanet Code
ORPHA:98896Duchenne Muscular Dystrophy
| ICD-10 | G71.01 |
| MeSH | D020388 |
| Orphanet | ORPHA:98896 |
| Treatments | 2 drug(s) |
| Symptoms on record | 15 signs |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO