Futibatinib

Orphan DrugFDA Approved

Description

Futibatinib is an oral irreversible FGFR1-4 inhibitor approved for previously treated unresectable locally advanced or metastatic intrahepatic cholangiocarcinoma with FGFR2 fusions or rearrangements. It is a precision-oncology orphan therapy with a narrow biomarker-defined population. This makes it a strong fit for rare-disease and specialty-access datasets.

Indications & Therapeutic Use

intrahepatic cholangiocarcinoma with FGFR2 fusion or rearrangement

Global Availability (2 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
Futibatinib
Generic Namefutibatinib
Brands1 brand available
Active Ingredientfutibatinib
Drug Classintrahepatic cholangiocarcinoma with FGFR2 fusion or rearrangement
ManufacturerTaiho Oncology
Dosage FormsOral tablet
Medical CodeL01EN
Orphan StatusYes — Orphan Drug
Cold ChainNot Required
Reg. StatusFDA Approved
Clinical TrialNCT02052778
Countries2 countries
Authority Signals
Last Verified7/24/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations3 Validated Nodes