Olipudase alfa
Orphan Drug Cold Chain RequiredFDA Approved
Contents
Description
Olipudase alfa is a recombinant human acid sphingomyelinase (ASM) enzyme. It is indicated for the treatment of non-central nervous system (CNS) manifestations of acid sphingomyelinase deficiency (ASMD), also known as Niemann-Pick disease type A/B and type B.
Indications & Therapeutic Use
Acid Sphingomyelinase Deficiency (ASMD)
Global Availability (2 countries)
| Country | Access Route | Regulatory Pathway | Lead Time | Status |
|---|---|---|---|---|
| — | — | — | — | |
| — | — | — | — |
Buy / Source Olipudase alfa — GNH India
8 matching products available through GNH India. Select a product to view details and request a quote on the GNH India website.
Browse all Olipudase alfa products on GNH IndiaProducts and ordering are fulfilled by GNH India. You will be redirected to www.gnhindia.com.
Available Through
This drug is available for procurement through the following fulfilment partner.
Fulfilment Partner
Olipudase alfa
| Generic Name | Olipudase alfa |
| Brands | 1 brand available |
| Active Ingredient | Olipudase alfa |
| Drug Class | Acid Sphingomyelinase Deficiency (ASMD) |
| Manufacturer | Sanofi Genzyme |
| Dosage Forms | Lyophilized powder for IV infusion |
| Medical Code | A16AB14 |
| Orphan Status | Yes — Orphan Drug |
| Cold Chain | Required |
| Lead Time | 14 days |
| Reg. Status | FDA Approved |
| Clinical Trial | NCT02004695 |
| Countries | 2 countries |
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations3 Validated Nodes