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OrphanDrug covers global rare drug access intelligence for 193 countries.

HomeDrugs

Orphan & Rare Drug Database

16 entries

All A B C D E F G H I J K L M N O P Q R S T U V W X Y Z

Orphan Drugs Only

Orphan14dInvestigational

mannose-1-phosphate

Orphan Cold Chain30dInvestigational

Orphan Cold ChainFDA Approved (2024)

Orphan14dFDA Approved

OrphanFDA Approved

Orphan Cold Chain14dFDA Approved, EMA Approved

Orphan7dEMA Approved, FDA OTC

Orphan3dFDA Approved

Orphan Cold Chain21dFDA Approved

Orphan14dFDA Approved

Orphan14dFDA Approved

OrphanFDA Approved

Orphan14dFDA Approved, EMA Approved

Orphan Cold ChainFDA Approved

OrphanFDA Approved (2025)

Orphan10dFDA Approved (2022), EMA Approved (2022)

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