Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
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Orphan & Rare Drug Database
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Orphan Drugs Only
Valproic Acid
7d
FDA Approved
vamorolone
Orphan
FDA Approved
vanzacaftor/tezacaftor/deutivacaftor
Orphan
FDA Approved (2024)
Vigabatrin
Orphan
14d
FDA Approved, EMA Approved
vimseltinib
Orphan
FDA Approved (2025)
Vinblastine
Cold Chain
FDA Approved
Vorasidenib
Orphan
14d
FDA Approved
vosoritide
Orphan
Cold Chain
21d
FDA Approved
vutrisiran
Orphan
Cold Chain
18d
FDA Approved (2022), EMA Approved (2022)
