Orphan & Rare Drug Database
23 entriesmannose
Orphan14d
mannose-1-phosphate
Orphan Cold Chain30d
marstacimab
Orphan Cold Chain
mavacamten
Orphan14d
mavorixafor
Orphan
mecasermin
Orphan Cold Chain14d
melatonin
Orphan7d
Melphalan
7d
Memantine
5d
Mesalamine
7d
Methotrexate
Orphan3d
metoprolol
2d
Metreleptin
Orphan Cold Chain21d
Metronidazole
3d
mexiletine
Orphan14d
Midostaurin
Orphan14d
Mifepristone
Orphan
miglustat
Orphan14d
minoxidil
5d
Mipomersen
Orphan Cold Chain
mirdametinib
Orphan
mitapivat
Orphan10d
mycophenolate mofetil
3d