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OrphanDrug covers global rare drug access intelligence for 193 countries.

HomeDrugs

Orphan & Rare Drug Database

280 entries

All A B C D E F G H I J K L M N O P Q R S T U V W X Y Z

Orphan Drugs Only

OrphanFDA Approved

vanzacaftor/tezacaftor/deutivacaftor

OrphanFDA Approved (2024)

Orphan14dFDA Approved, EMA Approved

OrphanFDA Approved (2025)

Cold ChainFDA Approved

Orphan14dFDA Approved

Orphan Cold Chain21dFDA Approved

Orphan Cold Chain18dFDA Approved (2022), EMA Approved (2022)

Zoledronic Acid

Cold Chain10dFDA Approved, EMA Approved

Page 10 of 10 (280 total)

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