Orphan & Rare Drug Database
280 entriesL-carnitine
Orphan5d
L-DOPA
L-Methylfolate
5d
Lanreotide
Orphan Cold Chain14d
laronidase
Orphan Cold Chain14d
Laser photocoagulation therapy
Orphan
Levetiracetam
3d
Levodopa/Carbidopa
7d
Lomitapide
Orphan
lonafarnib
Orphan21d
loncastuximab tesirine
Orphan Cold Chain14d
Lorenzo's oil
Lumasiran
Orphan Cold Chain
luspatercept
Orphan Cold Chain10d
mannose
Orphan14d
mannose-1-phosphate
Orphan Cold Chain30d
marstacimab
Orphan Cold Chain
mavacamten
Orphan14d
mavorixafor
Orphan
mecasermin
Orphan Cold Chain14d
melatonin
Orphan7d
Melphalan
7d
Memantine
5d
Mesalamine
7d
Methotrexate
Orphan3d
metoprolol
2d
Metreleptin
Orphan Cold Chain21d
Metronidazole
3d
mexiletine
Orphan14d
Midostaurin
Orphan14d