Pharma Knowledge Layer · Global Orphan Drug Access Intelligence

Pharma Knowledge Base

Orphan & Rare Drug Database

146 entries

All A B C D E F G H I J K L M N O P Q R S T U V W X Y Z

Orphan Drugs Only

mannose-1-phosphate

Orphan Cold Chain30dInvestigational

Orphan Cold ChainFDA Approved (2024)

Orphan14dFDA Approved

OrphanFDA Approved

Orphan Cold Chain14dFDA Approved, EMA Approved

Orphan7dEMA Approved, FDA OTC

Orphan3dFDA Approved

Orphan Cold Chain21dFDA Approved

Orphan14dFDA Approved

Orphan14dFDA Approved

OrphanFDA Approved

Orphan14dFDA Approved, EMA Approved

Orphan Cold ChainFDA Approved

OrphanFDA Approved (2025)

Orphan10dFDA Approved (2022), EMA Approved (2022)

Orphan21dFDA Approved

Orphan Cold ChainFDA Approved

Orphan Cold Chain7dUnregistered in India

Orphan Cold Chain10dFDA Approved

Orphan Cold ChainFDA Approved (2024)

Orphan Cold Chain14dFDA Approved

Onasemnogene abeparvovec

Orphan Cold Chain14dNot registered in India

Orphan14dFDA Approved

Orphan Cold ChainFDA Approved

OrphanFDA Approved

Orphan Cold ChainFDA Approved

Orphan Cold ChainFDA Approved (2024)

Orphan7dFDA Approved

Orphan7dUnregistered in India

Orphan Cold Chain14dFDA Approved

Page 4 of 5 (146 total)

← Prev Next →